Curing peripheral nerve diseases with genetic medicine
Our mission is to turn the promise of genetic therapies into cures for people living with peripheral nerve diseases, starting with Neurofibromatosis type 1 (NF1).
180 million
people live with Peripheral Nerve Diseases
3 million
have Neurofibromatosis type 1
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Leadership
Gonzalo is a serial entrepreneur in advanced therapies, having founded three companies and led operations as COO for +5 years. He achieved one exit, and earned a UK-Spain Business Award. He holds a PhD in Molecular Oncology.
Liron has 13+ years of experience in gene therapy, having led the development of a hemophilia gene therapy at Spark Therapeutics, later licensed to Roche. She is co-founder of Noga Therapeutics and holds a PhD in Molecular Genetics.
Kerstin is Director of Pharma at Deep Science Ventures. She has built and launched over a dozen biotechs in advanced therapies. She was recently recognized as impactful female leader by the Global Leader Magazine.
Montse has 25+ years of experience in pharma, having served as Chief of Sustainability at Novartis. She advises executives and boards and co-chairs the Business Advisory Council of the Children’s Tumor Foundation.
Scientific Advisory Board
Principal Investigator of the Hereditary Cancer Group at IGTP with +25 years of experience in NF1 research.
Former VP of Nonclinical at Peel Therapeutics, Aleah brings deep strategic biotech expertise and, as an NF1 mother, personal insight into the cause.
Principal Investigator at UPenn Dept of Medicine, pioneering novel LNP-based therapeutics for chronic and rare diseases.
Our values
Patients
Everything we do starts with listening to the patient. Their needs, challenges, and experiences are our greatest source of inspiration.
Innovation
We believe in bold ideas, brave solutions, and technology that creates meaningful impact.
Focus
We know where we’re going. We focus on what truly matters to achieve results that make a significant difference.
Integrity
We act with honesty, transparency, and respect.
Continuous Growth
Our culture is built on continuous growth, service, and joy: as individuals, as a team, and as a company